CureAccelerator Live!, Current Research, Dr. Gordon, Drug, Minority/Underserved, Oncology, Pediatric, Rare, The University of Texas MD Anderson Cancer Center
Enhancing Treatment Response in Recurrent/Metastatic Osteosarcoma with Hydroxychloroquine Principal Investigator: Dr. Nancy Gordon Disease: Osteosarcoma Research Description: Osteosarcoma (OS) is an orphan disease affecting approximately 400 children and adolescents...
CureAccelerator Live!, Current Research, Dr. Teng, Drug, Pediatric, Rare, Stanford University
Treating Vascular Malformations Using the Cancer Drug Trametinib Principal Investigator: Dr. Joyce Teng Disease: Extracranial arteriovenous malformations Research Description: Extracranial arteriovenous malformation (AVM) is a network of abnormal blood vessels more...
CureAccelerator Live!, Current Research, Dr. Rower, Drug, Hearing Loss, Infectious Disease, Inner Ear, Pediatric, Rare, University of Utah
Repurposing the Antiviral Drug Valganciclovir to Treat Cytomegalovirus-Induced Hearing Loss Principal Investigator: Dr. Joseph Rower Disease: Hearing loss Research Description: Almost 400 children die each year from congenital cytomegalovirus (cCMV) infections, and...
Big Leap Research, Current Research, Developing World, Dr. Nguyen, Drug, Minority/Underserved, Pediatric, Rare, ReGRoW, Vietnam National Children’s Hospital
Improving Outcomes for the Rare Liver Disease Biliary Atresia with a Cancer Drug in Vietnam Principal Investigator: Dr. Anh-Hoa Pham Nguyen Disease: Biliary atresia Research Description: Biliary atresia (BA) is a rare congenital liver disease that causes bile duct...
Chicago, CureAccelerator Live!, Current Research, Dr. Lieber, Drug, Neuro, Pediatric
Repurposing a Blood Cancer Treatment to Treat Muscle Contractures in Cerebral Palsy Patients Principal Investigator: Dr. Richard Lieber Disease: Cerebral palsy Research Description: Cerebral palsy (CP) is the most common cause of childhood motor disability, affecting...
Children's Hospital of Philadelphia, Current Research, Diagnostic, Dr. Seif, Drug, Mid-Atlantic, Oncology, Pediatric, Rare
Preventing Relapse After Bone Marrow Transplant in Pediatric Acute Lymphoblastic Leukemia (ALL) with a Personalized Treatment Principal Investigator: Dr. Alix Seif Disease: Acute Lymphoblastic Leukemia Research Description: Pediatric acute lymphoblastic leukemia (ALL)...
