Children's National Research Institute, Current Research, Dr. Shur, Drug, Health Disparities, Mid-Atlantic, Minority/Underserved, Pediatric, Rare
Using Steroids to Improve Rhabdomyolysis Outcomes in Pediatric Patients Principal Investigator: Dr. Natasha Shur Condition: Rhabdomyolysis Research Description: Rhabdomyolysis is a rare disease characterized by muscle breakdown, resulting in damaged muscle tissues...
Children's Hospital of Philadelphia, Current Research, Diagnostic, Dr. Seif, Drug, Mid-Atlantic, Oncology, Pediatric, Rare
Preventing Relapse After Bone Marrow Transplant in Pediatric Acute Lymphoblastic Leukemia (ALL) with a Personalized Treatment Principal Investigator: Dr. Alix Seif Disease: Acute Lymphoblastic Leukemia Research Description: Pediatric acute lymphoblastic leukemia (ALL)...
Current Research, Developing World, Dr. Chang, Drug, George Washington University, Infectious Disease, LMICs, Mid-Atlantic, Minority/Underserved, Pediatric
Repurposing a Flu Treatment for Severe Dengue Patients in Colombia Principal Investigator: Dr. Aileen Chang Disease: Dengue Fever Research Description:Dengue viruses (DenV) are among the leading causes of pediatric morbidity and mortality globally, with 96 million...
Children's Hospital of Philadelphia, Completed Research, Dr. Levine, Dr. Sochett, Drug, Metabolic Disorder, Mid-Atlantic, Pediatric, Rare, The Hospital for Sick Children
Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism Principal Investigator: Dr. Michael Levine, Dr. Étienne Sochett Disease: CYP24A1 mutations, hypercalcemia, hypercalciuria Research Description: Patients with loss of function mutations in the CYP24A1...
Adult, Completed Research, Dr. Kim, Mid-Atlantic, Nutraceutical, Ophthalmic, University of Pennsylvania Medicine
Repurposing a Nutraceutical to Treat a Type of Age-Related Macular Degeneration Principal Investigator: Dr. Benjamin Kim Disease: Macular Degeneration Research Description: The retina is the light sensing tissue that lines the inside of the back of the eye. In the...
Completed Research, Dr. Riggins, Drug, Johns Hopkins Medicine, Mid-Atlantic, Oncology, Pediatric, Rare
A Phase I Trial for Recurrent Pediatric Brain Cancers Using a Repurposed Generic Drug Principal Investigator: Dr. Gregory Riggins Disease: Medulloblastoma, Glioblastoma Research Description: Medulloblastoma is the most common malignant brain tumor in children, and...
