CureAccelerator Live!, Current Research, Dr. Teng, Drug, Pediatric, Rare, Stanford University
Treating Vascular Malformations Using the Cancer Drug Trametinib Principal Investigator: Dr. Joyce Teng Disease: Extracranial arteriovenous malformations Research Description: Extracranial arteriovenous malformation (AVM) is a network of abnormal blood vessels more...
CureAccelerator Live!, Current Research, Dr. Rower, Drug, Hearing Loss, Infectious Disease, Inner Ear, Pediatric, Rare, University of Utah
Repurposing the Antiviral Drug Valganciclovir to Treat Cytomegalovirus-Induced Hearing Loss Principal Investigator: Dr. Joseph Rower Disease: Hearing loss Research Description: Almost 400 children die each year from congenital cytomegalovirus (cCMV) infections, and...
Combo, Current Research, Drug, Oncology, Pre-clinical, Prof. Allen, Rare, University of Cambridge
Testing two generic drugs to improve outcomes in osteosarcoma, a rare bone cancer Principal Investigator: Prof. Matthew Allen Disease: Osteosarcoma Research Description: Although osteosarcoma (OSA) is a rare type of cancer, it is the most common bone cancer in...
Big Leap Research, Current Research, Developing World, Dr. Nguyen, Drug, Minority/Underserved, Pediatric, Rare, ReGRoW, Vietnam National Children’s Hospital
Improving Outcomes for the Rare Liver Disease Biliary Atresia with a Cancer Drug in Vietnam Principal Investigator: Dr. Anh-Hoa Pham Nguyen Disease: Biliary atresia Research Description: Biliary atresia (BA) is a rare congenital liver disease that causes bile duct...
Adult, CureAccelerator Live!, Current Research, Dr. Phillips, Drug, Minority/Underserved, Oncology, Rare, University of Michigan
Improving Patient Response in Mantle Cell Lymphoma with Venetoclax Principal Investigator: Dr. Tycel Phillips Disease: Mantle cell lymphoma Research Description: Mantle cell lymphoma (MCL) is a rare form of non-Hodgkin lymphoma (NHL) that is diagnosed mostly in older...
Adult, Current Research, Dr. Grimes, Drug, Inner Ear, Pre-clinical, Stanford University
Modulating inner ear fluid regulation to treat Meniere’s disease Principal Investigator: Kevin Grimes, MD Disease: Meniere’s disease Research Description: Meniere’s disease affects approximately 600,000 patients in the United States alone, yet there is no cure...
