Research and News Involving:
Pediatric
Adult, Clinical Trials, Dr. Nichols, Drug, Oncology, Pediatric, Press Release, Rare Disease, St. Jude Children's Research Hospital
Press Release: St. Jude Researcher Wins CureAccelerator Live! for Rare Diseases St. Jude Researcher Wins CureAccelerator Live! for Rare Diseases Clinical Trial for Ultrarare Hemophagocytic Lymphohistiocytosis Receives Funding to Repurpose Existing Blood Cancer...
Adult, Clinical Trials, Dr. Nichols, Drug, Oncology, Pediatric, Press Release, Rare Disease, St. Jude Children's Research Hospital
Press Release: Finalists Announced for CureAccelerator Live! for Rare Diseases Competition Finalists Announced for CureAccelerator Live! for Rare Diseases Competition Pitch Event on June 6 in Philadelphia Features 4 Clinical Repurposing Projects April 3, 2019 Cures...
Adult, Children's Hospital of Philadelphia, Clinical Trials, Dr. Fleischman, Dr. Park, Dr. Phillips, Dr. Seif, Drug, Mid-Atlantic, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, University of California Davis, University of California Irvine, University of Michigan
Press Release: University of California, Irvine Researcher Wins CureAccelerator Live! for Rare Diseases University of California, Irvine Researcher Wins CureAccelerator Live! for Rare Diseases Clinical Trial in Myeloproliferative Neoplasms Receives Funding to...
Adult, Brigham Young University, Clinical Trials, Dr. Ghosh, Dr. Ito, Dr. Ohanian, Dr. Romancik, Dr. Watt, Drug, Emory University, Oncology, Pediatric, Press Release, Rare Disease, The University of Texas MD Anderson Cancer Center, University of Michigan, University of Pittsburgh
Press Release: Five clinical trials impacting blood cancers approved for funding Five clinical trials impacting blood cancers approved for funding Cures Within Reach partnered with Goldman Philanthropic Partnerships, Leukemia Research Foundation and individual donors...
Adult, Baylor College of Medicine, Brown University, Children's National Research Institute, Clinical Trials, Dr. Amorim, Dr. Holder, Dr. Shur, Drug, Health Disparities, Health Equity, Neurology, Oncology, Pediatric, Press Release, Rare Disease, University of California San Francisco
Press Release: Brown University and UCSF Researchers Win CureAccelerator Live! for Diversity, Equity & Inclusion Brown University and UCSF Researchers Win CureAccelerator Live! for Diversity, Equity & Inclusion Clinical Repurposing Trials in Bladder Cancer...
Clinical Trials, Dr. Gordon, Dr. Rower, Dr. Teng, Health Equity, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, The University of Texas MD Anderson Cancer Center, University of Utah
Press Release: Stanford and MD Anderson Researchers Both Win CureAccelerator Live! for Pediatric Rare Diseases Stanford and MD Anderson Researchers Both Win CureAccelerator Live! for Pediatric Rare Diseases Clinical Repurposing Trials in Vascular Malformations and...
Adult, Clinical Trials, DEBRA Chile, Dr. Gordon, Dr. Rower, Dr. Teng, Drug, Health Equity, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, The University of Texas MD Anderson Cancer Center, University of Utah
Press Release: Finalists Announced for Pediatric-Focused CureAccelerator Live! for Rare Diseases 2021 Competition Finalists Announced for Pediatric-Focused CureAccelerator Live! for Rare Diseases 2021 Competition Virtual Pitch Event on June 10 Features 4 Pediatric...
Adult, Clinical Trials, Dr. Chang, Dr. Mehta, Dr. Osman, Drug, Emory University, George Washington University, Health Equity, Infectious Disease, LMICs, Openbiome, Pediatric, Press Release, SIDS Hospital and Research Centre
Press Release: OpenBiome Researcher Wins CureAccelerator Live! for the Developing World OpenBiome Researcher Wins CureAccelerator Live! for the Developing World Clinical Trial for Severe Acute Malnutrition Receives Funding to Repurpose Existing Fecal Microbiota...
Adult, Clinical Trials, Dr. Chang, Dr. Mehta, Dr. Osman, Drug, Health Equity, Infectious Disease, LMICs, Oncology, Openbiome, Pediatric, Press Release, SIDS Hospital and Research Centre
Press Release: Finalists Announced for CureAccelerator Live! Competition, Impacting Patients in Developing World Finalists Announced for CureAccelerator Live! Competition, Impacting Patients in Developing World Pitch Event on May 23 in Boston Features 5 Medical...
Adult, Current Research, Dermatology, Dr. Johnson, Drug, Health Equity, Infectious Disease, LMICs, Pediatric, ReGRoW, Université d'Abomey-Calavi
Adding Beta-lactam Antibiotics to Shorten Buruli Ulcer Disease Therapy in Benin Principal Investigator: Dr. Roch Christian Johnson Disease: Buruli ulcer Research Description: Buruli ulcer (BU), a neglected tropical disease, is a chronic debilitating mycobacterial...
Completed Research, Dr. Namazzi, Early Stage Investigator, Global Health Uganda, Health Equity, Inherited Disorder, LMICs, Nutraceutical, Pediatric, ReGRoW
Adding Zinc to Reduce Sickle Cell Anemia-related Infections in Ugandan Children Principal Investigator: Dr. Ruth Namazzi Disease: Sickle Cell Anemia Research Description: Sickle cell anemia (SCA) is the most common inherited blood disease worldwide, and African...
Adult, Busitema University, Completed Research, Dr. Musaba, Drug, Health Equity, LMICs, Maternal Health, Pediatric, ReGRoW, Women's Health
Using Sodium Bicarbonate to Reduce Maternal / Fetal Death from Acidosis During Obstructed Labor in Uganda Principal Investigator: Dr. Milton Musaba Disease: Obstructed Labor Research Description: Obstructed labor (OL) poses a serious risk to both mother and infant,...
Children's National Research Institute, Current Research, Dr. Shur, Drug, Health Disparities, Health Equity, Mid-Atlantic, Pediatric, Rare Disease
Using Steroids to Improve Rhabdomyolysis Outcomes in Pediatric Patients Principal Investigator: Dr. Natasha Shur Condition: Rhabdomyolysis Research Description: Rhabdomyolysis is a rare disease characterized by muscle breakdown, resulting in damaged muscle tissues...
Chicago, Current Research, Dr. Wesevich, Drug, Early Stage Investigator, Health Disparities, Health Equity, Inherited Disorder, Pediatric, Rare Disease, University of Chicago
Testing a Low-Dose Anti-inflammatory Drug (Tocilizumab) for Acute Chest Syndrome in Sickle Cell Disease Principal Investigator: Dr. Austin Wesevich Condition: acute chest syndrome in sickle cell disease Research Description: Sickle cell disease (SCD) is a rare...
Current Research, Dr. Ohanian, Drug, Oncology, Pediatric, Rare Disease, The University of Texas MD Anderson Cancer Center
Adding Metal Detoxification Drugs to Improve Childhood AML and Other Blood Cancer Outcomes Principal Investigator: Dr. Maro Ohanian Disease: Pediatric, adolescent and young adult Acute Myeloid Leukemia, Myelodysplastic Syndrome and Acute Lymphoblastic Leukemia...
Completed Research, Dr. Jatto, Drug, Ear Nose Throat, Health Equity, Hearing Loss, Infectious Disease, LMICs, Pediatric, ReGRoW, University College Hospital Ibadan
Repurposing a Widely Available Antiseptic in Pediatric Chronic Ear Infections in Nigeria Principal Investigator: Dr. Mercy Jatto Disease: Chronic suppurative otitis media Research Description: Chronic suppurative otitis media (CSOM) is inflammation of the lining of...
Completed Research, CureAccelerator Live!, Dr. Gordon, Drug, Health Equity, Oncology, Pediatric, Rare Disease, The University of Texas MD Anderson Cancer Center
Enhancing Treatment Response in Recurrent/Metastatic Osteosarcoma with Hydroxychloroquine Principal Investigator: Dr. Nancy Gordon Disease: Osteosarcoma Research Description: Osteosarcoma (OS) is an orphan disease affecting approximately 400 children and adolescents...
Completed Research, CureAccelerator Live!, Dr. Teng, Drug, Pediatric, Rare Disease, Stanford University, Vascular
Treating Vascular Malformations Using the Cancer Drug Trametinib Principal Investigator: Dr. Joyce Teng Disease: Extracranial arteriovenous malformations Research Description: Extracranial arteriovenous malformation (AVM) is a network of abnormal blood vessels more...
Completed Research, CureAccelerator Live!, Dr. Rower, Drug, Ear Nose Throat, Hearing Loss, Infectious Disease, Inner Ear, Pediatric, Rare Disease, University of Utah
Repurposing the Antiviral Drug Valganciclovir to Treat Cytomegalovirus-Induced Hearing Loss Principal Investigator: Dr. Joseph Rower Disease: Hearing loss Research Description: Almost 400 children die each year from congenital cytomegalovirus (cCMV) infections, and...
Big Leap Research, Current Research, Dr. Nguyen, Drug, Health Equity, Liver Disease, LMICs, Pediatric, Rare Disease, ReGRoW, Vietnam National Children’s Hospital
Improving Outcomes for the Rare Liver Disease Biliary Atresia with a Cancer Drug in Vietnam Principal Investigator: Dr. Anh-Hoa Pham Nguyen Disease: Biliary atresia Research Description: Biliary atresia (BA) is a rare congenital liver disease that causes bile duct...