Research and News Involving:
Completed Research




Repurposing Bone Marrow Stem Cell Therapy for Vision Loss Caused by Retinitis Pigmentosa

Repurposing Bone Marrow Stem Cell Therapy for Vision Loss Caused by Retinitis Pigmentosa Principal Investigator: Dr. Susanna Park​ Disease: Retinitis Pigmentosa Research Description: Retinitis pigmentosa (RP) is a rare hereditary form of retinal degeneration that can...



Investigating the Effects of Repurposed Diuretic, Steroid and Immunosuppressive Drugs in Meniere’s Disease

Investigating the Effects of Repurposed Diuretic, Steroid and Immunosuppressive Drugs in Meniere’s Disease Principal Investigator: Dr. Shresh Pathak​ Disease: Meniere’s disease Research Description: Meniere’s disease (MD) is a disease that affects mainly adults and...




Using a Cancer Drug to Treat a Rare Pediatric Liver Disease

Using a Cancer Drug to Treat a Rare Pediatric Liver Disease Principal Investigator: Dr. Evan Nadler, Dr. Ai-Xuan Holterman​ Disease: Biliary Atresia Research Description: Biliary atresia (BA) is a rare disease, occurring in approximately 1 in 10,000-20,000 live...

Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism

Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism Principal Investigator: Dr. Michael Levine, Dr. Étienne Sochett Disease: CYP24A1 mutations, hypercalcemia, hypercalciuria Research Description: Patients with loss of function mutations in the CYP24A1...