Research and News Involving:
Completed Research





Investigating the Effects of Repurposed Diuretic, Steroid and Immunosuppressive Drugs in Meniere’s Disease

Investigating the Effects of Repurposed Diuretic, Steroid and Immunosuppressive Drugs in Meniere’s Disease Principal Investigator: Dr. Shresh Pathak​ Disease: Meniere’s disease Research Description: Meniere’s disease (MD) is a disease that affects mainly adults and...




Using a Cancer Drug to Treat a Rare Pediatric Liver Disease

Using a Cancer Drug to Treat a Rare Pediatric Liver Disease Principal Investigator: Dr. Evan Nadler, Dr. Ai-Xuan Holterman​ Disease: Biliary Atresia Research Description: Biliary atresia (BA) is a rare disease, occurring in approximately 1 in 10,000-20,000 live...

Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism

Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism Principal Investigator: Dr. Michael Levine, Dr. Étienne Sochett Disease: CYP24A1 mutations, hypercalcemia, hypercalciuria Research Description: Patients with loss of function mutations in the CYP24A1...












Repurposing a Blood Cancer Drug to Treat an Immune Disorder (HLH) in Children

Repurposing a Blood Cancer Drug to Treat an Immune Disorder (HLH) in Children Principal Investigator: Dr. Kim Nichols Disease: Hemophagocytic Lymphohistiocytosis Research Description: Hemophagocytic lymphohistiocytosis (HLH) is a rare, poorly understood disorder of...