Research and News Involving:
Rare Disease
Adult, Children's Hospital of Philadelphia, Clinical Trials, Dr. Fleischman, Dr. Park, Dr. Phillips, Dr. Seif, Drug, Mid-Atlantic, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, University of California Davis, University of California Irvine, University of Michigan
Press Release: University of California, Irvine Researcher Wins CureAccelerator Live! for Rare Diseases University of California, Irvine Researcher Wins CureAccelerator Live! for Rare Diseases Clinical Trial in Myeloproliferative Neoplasms Receives Funding to...
Adult, Brigham Young University, Clinical Trials, Dr. Ghosh, Dr. Ito, Dr. Ohanian, Dr. Romancik, Dr. Watt, Drug, Emory University, Oncology, Pediatric, Press Release, Rare Disease, The University of Texas MD Anderson Cancer Center, University of Michigan, University of Pittsburgh
Press Release: Five clinical trials impacting blood cancers approved for funding Five clinical trials impacting blood cancers approved for funding Cures Within Reach partnered with Goldman Philanthropic Partnerships, Leukemia Research Foundation and individual donors...
Adult, Baylor College of Medicine, Brown University, Children's National Research Institute, Clinical Trials, Dr. Amorim, Dr. Holder, Dr. Shur, Drug, Health Disparities, Health Equity, Neurology, Oncology, Pediatric, Press Release, Rare Disease, University of California San Francisco
Press Release: Brown University and UCSF Researchers Win CureAccelerator Live! for Diversity, Equity & Inclusion Brown University and UCSF Researchers Win CureAccelerator Live! for Diversity, Equity & Inclusion Clinical Repurposing Trials in Bladder Cancer...
Adult, Cincinnati Children's Hospital Medical Center, Clinical Trials, Device, Drug, Emory University, Health Disparities, Health Equity, LMICs, Neurology, Oncology, Press Release, Rare Disease, SIDS Hospital and Research Centre, Stanford University, University College Hospital Ibadan, University of California Los Angeles, University of Illinois at Chicago
Press Release: Cures Within Reach seeks clinical trials in health disparities or led by underserved researchers Cures Within Reach seeks clinical trials in health disparities or led by underserved researchers Ten clinical trials starting soon in Diversity, Equity...
Clinical Trials, Dr. Gordon, Dr. Rower, Dr. Teng, Health Equity, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, The University of Texas MD Anderson Cancer Center, University of Utah
Press Release: Stanford and MD Anderson Researchers Both Win CureAccelerator Live! for Pediatric Rare Diseases Stanford and MD Anderson Researchers Both Win CureAccelerator Live! for Pediatric Rare Diseases Clinical Repurposing Trials in Vascular Malformations and...
Adult, Clinical Trials, DEBRA Chile, Dr. Gordon, Dr. Rower, Dr. Teng, Drug, Health Equity, Oncology, Pediatric, Press Release, Rare Disease, Stanford University, The University of Texas MD Anderson Cancer Center, University of Utah
Press Release: Finalists Announced for Pediatric-Focused CureAccelerator Live! for Rare Diseases 2021 Competition Finalists Announced for Pediatric-Focused CureAccelerator Live! for Rare Diseases 2021 Competition Virtual Pitch Event on June 10 Features 4 Pediatric...
Adult, Chicago, Clinical Trials, Dr. Liotta, Dr. Meltzer, Dr. Rado, Drug, Edward Hines Jr. VA Hospital and CARES, Health Disparities, Infectious Disease, Loyola University Medical Center, Military/Veteran, Neurology, Northwestern University, Oncology, Press Release, Rare Disease, Shirley Ryan AbilityLab, University of Chicago, Women's Health
Press Release: Clinical Repurposing Trials for COVID-19 and Cerebral Palsy Underway in Chicago Clinical Repurposing Trials for COVID-19 and Cerebral Palsy Underway in Chicago Trials at the University of Chicago, Northwestern University and Shirley Ryan AbilityLab...
Adult, Chicago, Clinical Trials, Dr. Liotta, Edward Hines Jr. VA Hospital and CARES, Loyola University Medical Center, Military/Veteran, Neurology, Northwestern University, Oncology, Press Release, Rare Disease, Shirley Ryan AbilityLab, Women's Health
Press Release: Finalists Announced for CureAccelerator Live! for Chicago 2020 Competition Finalists Announced for CureAccelerator Live! for Chicago 2020 Competition Virtual Pitch Event on September 15 Features 4 Clinical Repurposing Projects from Chicago Region July...
Adult, Chicago, Current Research, Device, Dr. Kletzel, Edward Hines Jr. VA Hospital and CARES, Military/Veteran, Neurology, Rare Disease
Improving Cognitive Function in Veterans with Atypical Parkinsonism with rTMS Brain Stimulation Principal Investigator: Dr. Sandra Kletzel Disease: Atypical Parkinsonism Research Description: Atypical parkinsonisms (APs) represent a group of progressive nervous system...
Adult, Current Research, Dr. Malichewe, Drug, Early Stage Investigator, Health Equity, LMICs, Muhimbili University Health and Allied Sciences, Oncology, Rare Disease, ReGRoW
Testing a Generic Drug Combination to Treat AML in Tanzania Principal Investigator: Dr. Christina Malichewe Disease: Acute Myeloid Leukemia Research Description: Acute myeloid leukemia (AML) is a blood cancer that is difficult to manage, and patients may have shorter...
Colorado State University, Completed Research, Dr. Regan, Drug, Oncology, Pre-clinical, Rare Disease
Evaluating an Approved Drug Combination Plus Immunotherapy in Canine Metastatic Osteosarcoma Principal Investigator: Dr. Daniel Regan Disease: Canine Metastatic Osteosarcoma Research Description: Metastasis remains the greatest challenge in osteosarcoma (OS) patient...
Adult, Current Research, Dr. Ghosh, Drug, Oncology, Rare Disease, University of Michigan
Reducing CAR T-cell Therapy Complications in Relapsed Lymphoma Patients by Adding Natalizumab Principal Investigator: Dr. Monalisa Ghosh Disease: Relapsed Lymphoma Research Description: Chimeric antigen receptor (CAR) T-cell therapy offers new hope through...
Adult, Brigham Young University, Current Research, Dr. Watt, Drug, Oncology, Rare Disease
Treating Anemia in Myelofibrosis with Nelfinavir Principal Investigator: Dr. Richard Watt Disease: Myelofibrosis Research Description: Patients with myelofibrosis, an incurable blood cancer, often have chronic inflammation, which results in high levels of the hormone...
Adult, City of Hope, Current Research, Dr. Phillips, Drug, Health Equity, Los Angeles, Oncology, Rare Disease
Repurposing Venetoclax and Glofitamab to Improve Patient Response in Mantle Cell Lymphoma Principal Investigator: Dr. Tycel Phillips Disease: Mantle cell lymphoma Research Description: Mantle cell lymphoma (MCL) is a rare form of non-Hodgkin lymphoma (NHL) that is...
Adult, Dr. Romancik, Drug, Emory University, Ended Early, Oncology, Rare Disease
Combining Approved Drugs for Alcoholism and Cancer to Treat Diffuse Large B-cell Lymphoma Principal Investigator: Dr. Jason Romancik Disease: Diffuse Large B-cell Lymphoma Research Description: Diffuse large B-cell lymphoma (DLBCL) and other aggressive subtypes of...
Children's National Research Institute, Current Research, Dr. Shur, Drug, Health Disparities, Health Equity, Mid-Atlantic, Pediatric, Rare Disease
Using Steroids to Improve Rhabdomyolysis Outcomes in Pediatric Patients Principal Investigator: Dr. Natasha Shur Condition: Rhabdomyolysis Research Description: Rhabdomyolysis is a rare disease characterized by muscle breakdown, resulting in damaged muscle tissues...
Chicago, Current Research, Dr. Wesevich, Drug, Early Stage Investigator, Health Disparities, Health Equity, Inherited Disorder, Pediatric, Rare Disease, University of Chicago
Testing a Low-Dose Anti-inflammatory Drug (Tocilizumab) for Acute Chest Syndrome in Sickle Cell Disease Principal Investigator: Dr. Austin Wesevich Condition: acute chest syndrome in sickle cell disease Research Description: Sickle cell disease (SCD) is a rare...
Adult, Completed Research, Dr. Ito, Drug, Oncology, Rare Disease, University of Pittsburgh
Investigating a Rare Disease Drug to Treat AML and MDS Patients with Post-Stem Cell Transplant Relapse Principal Investigator: Dr. Sawa Ito Disease: Acute Myeloid Leukemia and Myelodysplastic Syndrome Research Description: Allogeneic hematopoietic stem cell...
Current Research, Dr. Ohanian, Drug, Oncology, Pediatric, Rare Disease, The University of Texas MD Anderson Cancer Center
Adding Metal Detoxification Drugs to Improve Childhood AML and Other Blood Cancer Outcomes Principal Investigator: Dr. Maro Ohanian Disease: Pediatric, adolescent and young adult Acute Myeloid Leukemia, Myelodysplastic Syndrome and Acute Lymphoblastic Leukemia...
Adult, Chicago, Completed Research, Device, Diagnostic, Dr. Sims, Health Disparities, Health Equity, Oncology, Rare Disease, University of Illinois at Chicago
Repurposing a Diagnostic Device to Address Health Disparities in Esophageal Cancer Screening and Outcomes Principal Investigator: Dr. H. Steven Sims Disease: Esophageal cancer Research Description: Esophageal cancer can be divided into two types: adenocarcinoma (the...