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Using a Cancer Drug to Treat a Rare Pediatric Liver Disease

Using a Cancer Drug to Treat a Rare Pediatric Liver Disease Principal Investigator: Dr. Evan Nadler, Dr. Ai-Xuan Holterman​ Disease: Biliary Atresia Research Description: Biliary atresia (BA) is a rare disease, occurring in approximately 1 in 10,000-20,000 live...

Treating Irritability in Huntington’s Disease with a Repurposed Neurological Drug

Treating Irritability in Huntington’s Disease with a Repurposed Neurological Drug Principal Investigator: Erin Furr-Stimming, MD   Disease: Huntington’s Disease Research Description: Huntington’s disease (HD) is a devastating inherited neurologic disease that...