Adult, Cardio, Chicago, Combo, Completed Research, CureAccelerator Live!, Device, Dr. Eton, Dr. Havelka, Drug, Longest Day of Golf, Vascular
Saving Limbs from Chronic Ischemia: Helping Nature Do Its Magic Principal Investigator: Dr. George Havelka, Dr. Darwin Eton Disease: Chronic limb-threatening ischemia Research Description: Patients with Chronic Limb‐threatening Ischemia (CLI) suffer from impeded...
Chicago, Children's National Health System, Completed Research, Dr. Holterman, Dr. Nadler, Drug, Liver Disease, Longest Day of Golf, Pediatric, Rare, Uncategorized, University of Illinois at Chicago
Using a Cancer Drug to Treat a Rare Pediatric Liver Disease Principal Investigator: Dr. Evan Nadler, Dr. Ai-Xuan Holterman Disease: Biliary Atresia Research Description: Biliary atresia (BA) is a rare disease, occurring in approximately 1 in 10,000-20,000 live...
Children's Hospital of Philadelphia, Completed Research, Dr. Levine, Dr. Sochett, Drug, Metabolic Disorder, Mid-Atlantic, Pediatric, Rare, The Hospital for Sick Children
Repurposing an Antibiotic to Treat a Defect in Vitamin D Metabolism Principal Investigator: Dr. Michael Levine, Dr. Étienne Sochett Disease: CYP24A1 mutations, hypercalcemia, hypercalciuria Research Description: Patients with loss of function mutations in the CYP24A1...
Adult, Completed Research, Dr. Kim, Mid-Atlantic, Nutraceutical, Ophthalmic, University of Pennsylvania Medicine
Repurposing a Nutraceutical to Treat a Type of Age-Related Macular Degeneration Principal Investigator: Dr. Benjamin Kim Disease: Macular Degeneration Research Description: The retina is the light sensing tissue that lines the inside of the back of the eye. In the...
Completed Research, Dr. Riggins, Drug, Johns Hopkins Medicine, Mid-Atlantic, Oncology, Pediatric, Rare
A Phase I Trial for Recurrent Pediatric Brain Cancers Using a Repurposed Generic Drug Principal Investigator: Dr. Gregory Riggins Disease: Medulloblastoma, Glioblastoma Research Description: Medulloblastoma is the most common malignant brain tumor in children, and...